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AML = acute myeloid leukemia; CAR-T = chimeric antigen receptor T cell; CML = chronic myeloid leukemia; GI = gastrointestinal; MDS = myelodysplastic syndromes; NET = neuroendocrine tumor; PNH = paroxysmal nocturnal hemoglobinuria; PROS = PIK3CA-related overgrowth spectrum.